- Review
Motor Outcome Measures in Pediatric Patients with Congenital Muscular Dystrophies: A Scoping Review
- Ilaria Cavallina,
- Rossella D’Alessandro,
- Chiara Brusa,
- Elisa Panero,
- Enrica Rolle,
- Francesca Rossi,
- Tiziana Mongini and
- Federica Silvia Ricci
Congenital muscular dystrophies (CMDs) are a heterogeneous group of genetic neuromuscular disorders. They usually occur at birth or in early childhood, with delayed acquisition of motor milestones, and diffuse muscle weakness. A dystrophic pattern is...

