Special Issue "Genome Editing Therapies"
Deadline for manuscript submissions: closed (15 October 2019).
Interests: musculoskeletal disease; facioscapulohumeral muscular dystrophy (FSHD); CRISPR/Cas9 genome-editing; BMP signaling; Fibrodysplasia Ossificans Progressiva (FOP)
Special Issues and Collections in MDPI journals
The recent advances in the development of genome editing technologies have significantly improved our ability to directly make changes in the genomes in a precise manner. A particularly attractive application of genome editing is the potential to directly correct genetic mutations for the treatment of currently incurable diseases. Genome-editing therapy has already shown promise in treating inherited genetic diseases, such as Duchenne muscular dystrophy. This Special Issue, Genome Editing Therapies, will focus on the recent progress in the development of novel therapies using genome editing technologies. We intend to invite researchers in the field to submit original research and review articles on the advancement of novel genome-editing therapies, including (but not limited to) the CRISPR-Cas /cpf1 system, TALEN, mutation-based personalized medicine, delivery enhancement, exosome-mediated delivery, off-target effects, bioinformatics, and disease models, to evaluate the efficacy of treatments.
Dr. Toshifumi Yokota
Dr. Rika Maruyama
Manuscript Submission Information
Manuscripts should be submitted online at www.mdpi.com by registering and logging in to this website. Once you are registered, click here to go to the submission form. Manuscripts can be submitted until the deadline. All papers will be peer-reviewed. Accepted papers will be published continuously in the journal (as soon as accepted) and will be listed together on the special issue website. Research articles, review articles as well as short communications are invited. For planned papers, a title and short abstract (about 100 words) can be sent to the Editorial Office for announcement on this website.
Submitted manuscripts should not have been published previously, nor be under consideration for publication elsewhere (except conference proceedings papers). All manuscripts are thoroughly refereed through a single-blind peer-review process. A guide for authors and other relevant information for submission of manuscripts is available on the Instructions for Authors page. International Journal of Molecular Sciences is an international peer-reviewed open access semimonthly journal published by MDPI.
Please visit the Instructions for Authors page before submitting a manuscript. There is an Article Processing Charge (APC) for publication in this open access journal. For details about the APC please see here. Submitted papers should be well formatted and use good English. Authors may use MDPI's English editing service prior to publication or during author revisions.
- genome editing
- guide RNA