Special Issue "New Insights in the Diagnosis and Treatment of Hemophilia"
A special issue of Journal of Clinical Medicine (ISSN 2077-0383). This special issue belongs to the section "Hematology".
Deadline for manuscript submissions: closed (1 March 2023) | Viewed by 2684
Special Issue Editors
Interests: hemophilia; prophylaxis; gene therapy; burden of illness; quality of life; patient reported outcomes
2. Department of Pediatrics, University of Illinois College of Medicine, Peoria, IL, USA
Interests: hemophilia; Von Willebrand disease; coagulation laboratory testing; hemostasis; thrombosis; platelet disorders; patient centered outcome measures; anticoagulation
Special Issue Information
Dear Colleagues,
Haemophilia diagnosis and treatment has evolved significantly in the last twenty years. Increasing attention is being paid to the burden of illness, quality of life, and treatment preferences for patients with this disorder. While principal outcomes frequently measure bleeds, joint arthropathy, and pain, other effects may be important to patients. Most importantly, there is recognition that this disorder has patients across the globe, and international efforts have advocated for broader treatment, and treatment options.
With the development of a variety of new treatments, it is essential that research on treatment outcomes be developed and assessed. In addition to clinical trials, observational studies can provide insight into treatment effects and predictors of success. The focus of this special issue is to report on new areas of treatment, new measurements being used to identify treatment effects, and treatment outcomes. The issue will also consider the potential impact of treatments presently under development, and how clinicians may adopt them.
Dr. Michael B. Nichol
Dr. Jonathan C. Roberts
Guest Editors
Manuscript Submission Information
Manuscripts should be submitted online at www.mdpi.com by registering and logging in to this website. Once you are registered, click here to go to the submission form. Manuscripts can be submitted until the deadline. All submissions that pass pre-check are peer-reviewed. Accepted papers will be published continuously in the journal (as soon as accepted) and will be listed together on the special issue website. Research articles, review articles as well as short communications are invited. For planned papers, a title and short abstract (about 100 words) can be sent to the Editorial Office for announcement on this website.
Submitted manuscripts should not have been published previously, nor be under consideration for publication elsewhere (except conference proceedings papers). All manuscripts are thoroughly refereed through a single-blind peer-review process. A guide for authors and other relevant information for submission of manuscripts is available on the Instructions for Authors page. Journal of Clinical Medicine is an international peer-reviewed open access semimonthly journal published by MDPI.
Please visit the Instructions for Authors page before submitting a manuscript. The Article Processing Charge (APC) for publication in this open access journal is 2600 CHF (Swiss Francs). Submitted papers should be well formatted and use good English. Authors may use MDPI's English editing service prior to publication or during author revisions.
Keywords
- hemophilia
- prophylaxis
- gene therapy
- burden of illness
- quality of life
- patient reported outcomes