Bara-Ledesma, N.; Viteri-Noel, A.; Lopez Rodriguez, M.; Stamatakis, K.; Fabregate, M.; Vazquez-Santos, A.; Gomez del Olmo, V.
Advances in Gene Therapy for Rare Diseases: Targeting Functional Haploinsufficiency Through AAV and mRNA Approaches. Int. J. Mol. Sci. 2025, 26, 578.
https://doi.org/10.3390/ijms26020578
AMA Style
Bara-Ledesma N, Viteri-Noel A, Lopez Rodriguez M, Stamatakis K, Fabregate M, Vazquez-Santos A, Gomez del Olmo V.
Advances in Gene Therapy for Rare Diseases: Targeting Functional Haploinsufficiency Through AAV and mRNA Approaches. International Journal of Molecular Sciences. 2025; 26(2):578.
https://doi.org/10.3390/ijms26020578
Chicago/Turabian Style
Bara-Ledesma, Nuria, Adrian Viteri-Noel, Monica Lopez Rodriguez, Konstantinos Stamatakis, Martin Fabregate, Almudena Vazquez-Santos, and Vicente Gomez del Olmo.
2025. "Advances in Gene Therapy for Rare Diseases: Targeting Functional Haploinsufficiency Through AAV and mRNA Approaches" International Journal of Molecular Sciences 26, no. 2: 578.
https://doi.org/10.3390/ijms26020578
APA Style
Bara-Ledesma, N., Viteri-Noel, A., Lopez Rodriguez, M., Stamatakis, K., Fabregate, M., Vazquez-Santos, A., & Gomez del Olmo, V.
(2025). Advances in Gene Therapy for Rare Diseases: Targeting Functional Haploinsufficiency Through AAV and mRNA Approaches. International Journal of Molecular Sciences, 26(2), 578.
https://doi.org/10.3390/ijms26020578