Tegsedi (Inotersen): An Antisense Oligonucleotide Approved for the Treatment of Adult Patients with Hereditary Transthyretin Amyloidosis
Abstract
:1. Introduction
2. Tegsedi (Inotersen)
2.1. Name
2.2. Uses
2.3. Mechanism of Action
2.4. Clinical Studies
3. Perspectives
Funding
Conflicts of Interest
References
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Gales, L. Tegsedi (Inotersen): An Antisense Oligonucleotide Approved for the Treatment of Adult Patients with Hereditary Transthyretin Amyloidosis. Pharmaceuticals 2019, 12, 78. https://doi.org/10.3390/ph12020078
Gales L. Tegsedi (Inotersen): An Antisense Oligonucleotide Approved for the Treatment of Adult Patients with Hereditary Transthyretin Amyloidosis. Pharmaceuticals. 2019; 12(2):78. https://doi.org/10.3390/ph12020078
Chicago/Turabian StyleGales, Luís. 2019. "Tegsedi (Inotersen): An Antisense Oligonucleotide Approved for the Treatment of Adult Patients with Hereditary Transthyretin Amyloidosis" Pharmaceuticals 12, no. 2: 78. https://doi.org/10.3390/ph12020078