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Journal: Pharmaceutics, 2026
Volume: 18
Number: 281
Article:
Liposomal CRISPR/Cas9-Mediated Local Genome Editing for Joint Disease in Mucopolysaccharidosis Type I
Authors:
by
Hallana Souza Santos, Edina Poletto, Luisa Natalia Pimentel Vera, Mirian Farinon, Francyne Kubaski, Paola Barcelos Carneiro, Willian da Silva Carniel, Roberto Giugliani, Ursula Matte, Helder Ferreira Teixeira, Roselena Silvestri Schuh and Guilherme Baldo
Link:
https://www.mdpi.com/1999-4923/18/3/281
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