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Journal: Int. J. Mol. Sci., 2025
Volume: 26
Number: 11282

Article: GAMT Deficiency: Clinical Presentation, Treatment, Diagnosis, Animal Models, Preclinical and Clinical Developments
Authors: by Sara Biagiotti, Elena Perla, Serafina Manila Guzzo, Manuela Tolve, Francesca Nardecchia, Luigia Rossi, Claudia Carducci, Tiziana Pascucci, Vincenzo Leuzzi and Mauro Magnani
Link: https://www.mdpi.com/1422-0067/26/23/11282

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